Breakthrough Single-Molecule Valve Controls Nanoscale,Scientists dream of using tiny molecules as building blocks to...
Rare Diseases
Solving mystery behind how nutrients enter cells,Mouse embryos, like the one depicted above, die...
Royal Society Entrepreneur brings industry expertise to science,Scientific research at the University of Nottingham...
Nursing Researcher to Study Private Infusion Clinics in Canada,With her research, Quinn Grundy aims...
New technique reduces mutation problem in gene therapy for safer editing,CRISPR-Cas9 is widely used...
Eshelman Institute for Innovation Accepting Pre-proposals for Therapeutic Grant Cycle,The Eshelman Institute for Innovation...
U.S. Food and Drug Administration approves CSL's HEMGENIX , first gene therapy for hemophilia...
Ending postcode lottery in newborn health screening,Today, on International Neonatal Screening Day, the Albanese...
DECIPHER database for rare diseases joins EMBL-EBI,Closer collaborations with EMBL-EBI data resources set to...
Biotech Stocks Facing FDA Decision In March 2023,As another month draws to a close,...
Molecular Biologist Michael Green Dies at 69,Beyond his achievements in academia, he also cofounded...
'Light up for Rare' once again brings bright colors to monuments and hope to...
Biogen's new CEO Chris Viehbacher looks to ads, patient outreach to boost promotion of...
PharmaEssentia's new Besremi campaign focuses on what counts,PharmaEssentia’s new campaign for drug Besremi manages...
With FDA approval for Filspari, Travere turns Bristol Myers castoff into unique drug for...
Alnylam runs rare disease awareness series on social media for European consumers,Alnylam is using...
Moderna runs new 'Voice of the Patient' video with mom likening the pandemic lockdown...
Scientists use Avatar's motion capture AI technology to diagnose rare diseases,Avatar's motion capture technology...
Genome Study Targets Rare Immune Disorders in Children,CU Anschutz-led research seeks genetic defects to...
Treatment Strategy Found for Bone Marrow Failure Syndrome,Bone marrow is the spongy tissue inside...